393 - Deciphering the Therapeutic Effect of Dynamin-2 Reduction in SPEG-Related Myopathy: Perspectives from Multi-Omics Analysis
Friday, April 25, 2025
5:30pm – 7:45pm HST
Qifei Li, University of Miami Miller School of Medicine and Holtz Children's Hospital, Miami, FL, United States; Shiyu Luo, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Jasmine Lin, Boston Children's Hospital, Boston, MA, United States; Haoyue Sheng, University of Miami, Miami, FL, United States; Madesh Ramesh, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Klaus Schmitz-Abe, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States; Pankaj B.. Agrawal, University of Miami Leonard M. Miller School of Medicine, Miami, FL, United States